A team of Chinese scientists has uncovered a hidden 3D structure in rice DNA that allows the crop to grow more grain while ...
The ability of immune cells—particularly CD8+ T cells—to launch a rapid burst of proliferation inside tumors is key to the ...
Arc Institute, Gladstone Institutes, and University of California, San Francisco, scientists have developed an epigenetic ...
These long-term findings in a large patient cohort show the sustained clinical efficacy and safety of autologous CD34+ hematopoietic stem-cell lentiviral gene therapy for ADA-SCID, indicating that it ...
A Washington man appeared to be destined to develop Alzheimer’s disease — but against all genetic odds, he has eluded the common dementia for decades. Researchers at the Washington University School ...
AUSTIN, Texas, Oct. 14, 2025 /PRNewswire/ -- Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing life-changing therapies for patients ...
Regeneron is clearing a regulatory path for its investigational gene therapy DB-OTO after an early phase study demonstrated hearing improvements in children with a genetic form of deafness. The data, ...
Genetic deficiency of otoferlin, a protein critical to synaptic transmission by the sensory hair cells of the ear, causes congenital deafness. Medicines to treat the condition are lacking; children ...
Each year, a small number of babies are born mostly, if not fully, deaf because one of their genes isn’t working. The gene normally makes a protein that the hairs in our inner ears need to relay sound ...
Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...